AAV vector-mediated correction of brain pathology in a mouse model of Niemann-Pick A disease
- Marco A. Passini
- , Shannon L. Macauley
- , Michael R. Huff
- , Tatyana V. Taksir
- , Jie Bu
- , I. Huan Wu
- , Peter A. Piepenhagen
- , James C. Dodge
- , Lamya S. Shihabuddin
- , Catherine R. O'Riordan
- , Edward H. Schuchman
- , Gregory R. Stewart
Research output: Contribution to journal › Article › peer-review
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