Higher dosing of alglucosidase alfa improves outcomes in children with Pompe disease: a clinical study and review of the literature
- Aleena A. Khan
- , Laura E. Case
- , Mrudu Herbert
- , Stephanie DeArmey
- , Harrison Jones
- , Kelly Crisp
- , Kanecia Zimmerman
- , Mai K. ElMallah
- , Sarah P. Young
- , Priya S. Kishnani
Research output: Contribution to journal › Article › peer-review
58
Scopus
citations